ESPE Yearbook of Paediatric Endocrinology

To read the full abstract: N Engl J Med 2017;377:1313-1315“In 2010, 5-year-old Emily Whitehead was diagnosed with acute lymphoblastic leukemia.” So begins this remarkable story of how Emily became the first child to receive CART-19 (chimeric antigen receptor T-cell) therapy. She remains alive and well, and her successful treatment re-energised a whole line of research &#8...