ESPE Yearbook of Paediatric Endocrinology

ESPE Yearbook of Paediatric Endocrinology

ISSN 1662-4009 (online)

Published by BioScientifica
Previous issue | Volume 19 | ESPEYB19 | Next issue

Yearbook of Paediatric Endocrinology 2022

14. Science and Medicine

New treatments

Previous section
Risk and Outcome
Table of contents
Next section
Genetics

ey0019.14-13 | New treatments

14.13. CRISPR-Cas9 in vivo gene editing for transthyretin amyloidosis

ey0019.14-14 | New treatments

14.14. A novel therapeutic strategy for skeletal disorders: Proof of concept of gene therapy for X-linked hypophosphatemia

Published by BioScientifica

ESPE Yearbook of Paediatric Endocrinology
ISSN 1662-4009 (Online)
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